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Gene Editing Used to Repair Inherited Mutation in Embryos

Oregon State Health and Science University researchers used the CRISPR/Cas9 gene-editing system to correct mutations within MYBPC3 in embryos. They targeted an autosomal dominant mutation in MYBPC3 leading to hypertrophic cardiomyopathy, which affects about one in every 500 people and is a common cause of sudden death in young people.

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